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review · 2025

Unraveling Rare Diseases: A Review of Gaucher Disease, Noonan Syndrome, and Laron Syndrome

Despite being uncommon on its own, rare diseases pose serious problems for patients, healthcare systems, and pharmaceutical research when taken as a whole.Th...

0 citationsDOI: https://doi.org/10.47583/ijpsrr.2025.v85i6.017Open accessPDF reported by metadataFull text reported by metadata
Unraveling Rare Diseases: A Review of Gaucher Disease, Noonan Syndrome, and Laron Syndrome