article · 2014
O136 A NOVEL, HYBRID RECOMBINANT AAV-piggyBac TRANSPOSON VECTOR PERMITS ROBUST LONG-TERM PHENOTYPE CORRECTION OF THE PROGRESSIVE FAMILIAL INTRAHEPATIC CHOLESTASIS TYPE 3 MOUSE MODEL IN VIVO
1 citationsDOI: https://doi.org/10.1016/s0168-8278(14)60138-0